Healthcare utilisation in children with SMA type 1 treated with nusinersen: a single centre retrospective review
Imran Ali, Francis J Gilchrist, William D Carroll, John Alexander, Sadie Clayton, Richa Kulshrestha, Tracey Willis, Martin Samuels
BMJ Paediatrics Open Dec 2019, 3 (1) e000572; DOI: 10.1136/bmjpo-2019-000572